5 Solutions to Overcome Challenges Conducting Rare Disease Epidemiology
Epidemiology and patient population dynamics are at the core of understanding any disease market. For rare diseases, getting a firm grasp of the disease prevalence and incidence, diagnosis rates, treatment rates, representation of clinically [...]
3 Key Insights for Rare Disease Drug Developers: GSD Type 1a
Rare disease market research that captures the voice of the patient is indispensable for understanding a rare disease market. Moreover, because treatment planning for rare diseases is often a process [...]
Hematologists Report A Strong Willingness To Prescribe Novartis’ Adakveo And Global Blood Therapeutics’ Oxbryta But Are Holding Back Due To COVID-19, Treatment Costs, And Patients Being Well-Managed On Current Therapy
A study with 50 U.S. hematologists reveals that approximately one-third have already prescribed Adakveo or Oxbryta Newton, MA., September 30, 2020 — Sickle cell disease (SCD) is a chronic, [...]
The Challenges of Pediatric to Adult Care Transitions for Sickle Cell Disease Patients
Young adulthood is one of the most exciting times in life. It is full of new experiences, challenges, freedoms, and responsibilities. Young adults living with a chronic medical condition have [...]
5 Solutions to Overcome Challenges Conducting Rare Disease Epidemiology
Epidemiology and patient population dynamics are at the core of understanding any disease market. For rare diseases, getting a firm grasp of the disease prevalence and incidence, diagnosis rates, treatment rates, representation of clinically [...]
3 Key Insights for Rare Disease Drug Developers: GSD Type 1a
Rare disease market research that captures the voice of the patient is indispensable for understanding a rare disease market. Moreover, because treatment planning for rare diseases is often a process [...]
Hematologists Report A Strong Willingness To Prescribe Novartis’ Adakveo And Global Blood Therapeutics’ Oxbryta But Are Holding Back Due To COVID-19, Treatment Costs, And Patients Being Well-Managed On Current Therapy
A study with 50 U.S. hematologists reveals that approximately one-third have already prescribed Adakveo or Oxbryta Newton, MA., September 30, 2020 — Sickle cell disease (SCD) is a chronic, [...]
The Challenges of Pediatric to Adult Care Transitions for Sickle Cell Disease Patients
Young adulthood is one of the most exciting times in life. It is full of new experiences, challenges, freedoms, and responsibilities. Young adults living with a chronic medical condition have [...]