Three Unmet Needs Defining HS Treatment
3 Key Insights for Rare Disease Drug Developers: GSD Type 1a
Rare disease market research that captures the voice of the patient is indispensable for understanding a rare disease market. Moreover, because treatment planning for rare diseases is often a process [...]
Three Developments That Will Irreversibly Shape the Sickle Cell Disease Therapy Market
Investment in R&D is set to deliver much-needed, potentially disease-modifying therapies for people with sickle cell disease (SCD), especially those with severe disease. Severe disease is characterized by frequent [...]
Seven Questions I Would Ask (and Answer) If I Were Developing a New Drug for Sickle Cell Disease
The last six months have delivered a wave of clinical, commercial, and regulatory developments regarding the treatment of sickle cell disease (SCD). Indeed, the U.S. launch of two new [...]