Rare disease market research that captures the voice of the patient is indispensable for understanding a rare disease market. Moreover, because treatment planning for rare diseases is often a process [...]
Investment in R&D is set to deliver much-needed, potentially disease-modifying therapies for people with sickle cell disease (SCD), especially those with severe disease. Severe disease is characterized by frequent [...]
The last six months have delivered a wave of clinical, commercial, and regulatory developments regarding the treatment of sickle cell disease (SCD). Indeed, the U.S. launch of two new [...]
